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UrduNanoscope received National Institutes of Health (NIH) support for restoring visual response by non-viral laser based targeted delivery of ambient-light activatable opsin into the retina
Tag: Gene Therapy
Optimal time to treat Huntington’s disease identified
The earliest brain changes due to Huntington’s disease can be detected 24 years before clinical symptoms show, according to a new UCL-led study. The researchers say their findings, published in The Lancet Neurology , could help with clinical trials by…
Optimal time to treat Huntington’s disease identified
The earliest brain changes due to Huntington’s disease can be detected 24 years before clinical symptoms show, according to a new UCL-led study. The researchers say their findings, published in The Lancet Neurology , could help with clinical trials by…
Scientists find genes to save ash trees from deadly beetle
An international team of scientists have identified candidate resistance genes that could protect ash trees from the Emerald Ash Borer (EAB), a deadly pest that is expected to kill billions of trees worldwide. In the new study, published today in…
New rare disease with own facial features, cardiac defects and developmental delay
TRAF7 syndrom: the firts forty-five patients
New rare disease with own facial features, cardiac defects and developmental delay
TRAF7 syndrom: the firts forty-five patients
GlycoNet welcomes $16.3 million renewed federal funding
This funding extension will support glycomics research to improve the quality of life of patients across Canada
Genetic testing among individuals with ASD
What The Study Did: Professional medical societies recommend certain genetic tests for individuals with autism spectrum disorder (ASD). This study looked at how common it was for nearly 1,300 individuals diagnosed with ASD to undergo these tests and the factors…
Genetic testing among individuals with ASD
What The Study Did: Professional medical societies recommend certain genetic tests for individuals with autism spectrum disorder (ASD). This study looked at how common it was for nearly 1,300 individuals diagnosed with ASD to undergo these tests and the factors…
The EU not ready for the release of Gene drive organisms into the environment
EU scientists are taking a closer look into the CRISPR/Cas-9-induced population-wide genetic modifications before introducing it into practice
The EU not ready for the release of Gene drive organisms into the environment
EU scientists are taking a closer look into the CRISPR/Cas-9-induced population-wide genetic modifications before introducing it into practice
Focused ultrasound opening brain to previously impossible treatments
University of Virginia researchers are pioneering the use of focused ultrasound to defy the brain’s protective barrier so that doctors could, at last, deliver many treatments directly into the brain to battle neurological diseases. The approach, the researchers hope, could…
Focused ultrasound opening brain to previously impossible treatments
University of Virginia researchers are pioneering the use of focused ultrasound to defy the brain’s protective barrier so that doctors could, at last, deliver many treatments directly into the brain to battle neurological diseases. The approach, the researchers hope, could…
Genetic doppelgaengers: Emory research provides insight into two neurological puzzles
c9 form of ALS and SCA36
Massachusetts Eye and Ear, Mass General advancing novel gene-based COVID-19 vaccine, AAVCOVID
AAVCOVID technology is unique in the vaccine field in its ability to scale and adapt rapidly
Genetic doppelgaengers: Emory research provides insight into two neurological puzzles
c9 form of ALS and SCA36
Massachusetts Eye and Ear, Mass General advancing novel gene-based COVID-19 vaccine, AAVCOVID
AAVCOVID technology is unique in the vaccine field in its ability to scale and adapt rapidly
Wyss Institute joins forces with Cytosurge to improve CRISPR multiplexing
Collaboration focuses on developing multiplexed gene editing approaches using single-cell nano-manipulation technology that maintains cell viability and fitness
‘Unnecessary’ genetic complexity: A spanner in the works?
Overlapping versions of our entire genetic history, present in every cell, complicate the delivery of precision medicine, researchers find
Wyss Institute joins forces with Cytosurge to improve CRISPR multiplexing
Collaboration focuses on developing multiplexed gene editing approaches using single-cell nano-manipulation technology that maintains cell viability and fitness
‘Unnecessary’ genetic complexity: A spanner in the works?
Overlapping versions of our entire genetic history, present in every cell, complicate the delivery of precision medicine, researchers find
Double bubbles pierce with less trouble
Two optical cavitation bubbles penetrate soft materials better than one
Double bubbles pierce with less trouble
Two optical cavitation bubbles penetrate soft materials better than one
Professor John Shine AC elected as Fellow of the Royal Society
For his scientific leadership and pioneering research in molecular genetics Garvan’s Professor John Shine AC, has been elected as Fellow of the Royal Society.
Professor John Shine AC elected as Fellow of the Royal Society
For his scientific leadership and pioneering research in molecular genetics Garvan’s Professor John Shine AC, has been elected as Fellow of the Royal Society.
Gene defects linked to eczema, wheeze and nasal disease among babies
Research shows ‘personalised’ medicine approach could dramatically improve patients’ lives
A step toward a better way to make gene therapies to attack cancer, genetic disorders
A UCLA-led research team today reports that it has developed a new method for delivering DNA into stem cells and immune cells safely, rapidly and economically. The method, described in the journal Proceedings of the National Academy of Sciences ,…
The most promising strategies for defeating coronavirus: A review stud
In an unprecedented effort, hundreds of thousands of researchers and clinicians worldwide are locked in a race against time to develop cures, vaccines, and better diagnostic tests for COVID-19, the illness caused by the virus SARS-CoV-2.
The most promising strategies for defeating coronavirus: A review study
In an unprecedented effort, hundreds of thousands of researchers and clinicians worldwide are locked in a race against time to develop cures, vaccines, and better diagnostic tests for COVID-19, the illness caused by the virus SARS-CoV-2. Over 1,650 articles on…
Sanfilippo C syndrome: New brain cell models to evaluate therapies
Fighting degenerative diseases
Rice wins fed grant to advance sickle cell disease therapy
Bioengineer Gang Bao studies genome-editing outcomes to enable a future clinical trial
Breakthrough in genome visualization
Faster and less memory-intensive method developed
University of Guelph develops effective way to replenish threatened plants
University of Guelph researchers used advanced cloning techniques to give the threatened Hill’s thistle a fighting chance.
Researchers pinpoint potential new therapeutic target for eye disease
Multi-disciplinary work led by researchers from Trinity College Dublin has pinpointed a potential new therapeutic target for treating retinal degeneration. The work has discovered that a protein (SARM1) involved in neuronal cell injury may also have a role in the…
Novel technology aims to improve treatment of neurological diseases
Princeton researchers are developing genetic “on” switches for use in gene therapy, the practice of delivering new genes to replace or assist ones that are faulty.
Simulations show how to make gene therapy more effective
Diseases with a genetic cause could, in theory, be treated by supplying a correct version of the faulty gene. However, in practice, delivering new genetic material to human cells is difficult. A promising method for the delivery of such genes…
Landmark 30-year study on Crigler-Najjar syndrome underscores the need for new therapies
A new study summarizes more than 30 years of clinical experience and describes the clinical course of 28 individuals with Crigler-Najjar syndrome
Researchers map mechanism to explain role of gene mutations in kidney disease
Study could pave the way for future targeted treatments for kidney disease
New 3D cultured cells mimic the progress of NASH
A research team led by scientists from Tokyo University of Agriculture and Technology (TUAT), Japan, has successfully established 3D cultured tissue that mimics liver fibrosis, a key characteristic of non-alcoholic steatohepatitis (NASH). For making the 3D culture, cells were collected…
Cancer research, the guardian of the genome has a new ally
A team of researchers of the University of Trento focused on a new molecular mechanism that works like a ‘switch’
A new mechanism triggering cell death and inflammation: A left turn that kills
Z-form nucleic acids are double-stranded DNA and RNA molecules with an unusual left-handed double helix structure, as opposed to the classical right-handed Watson-Crick double helix. Z-nucleic acids were discovered more than 40 years ago, but their biological function has remained…
Cancer research, the guardian of the genome has a new ally
A team of researchers of the University of Trento focused on a new molecular mechanism that works like a ‘switch’
A new mechanism triggering cell death and inflammation: A left turn that kills
Z-form nucleic acids are double-stranded DNA and RNA molecules with an unusual left-handed double helix structure, as opposed to the classical right-handed Watson-Crick double helix. Z-nucleic acids were discovered more than 40 years ago, but their biological function has remained…
Benefiting from the national gene vector biorepository
New Rochelle, NY, March 26, 2020–Gene therapy investigators can greatly benefit from the resources and services provided by the National Gene Vector Biorepository (NGVB), housed at the Indiana University School of Medicine. These include 93 unique reagents, a searchable database…
Scientists identify gene that first slows, then accelerates, progression of ALS in mice
Columbia study underscores complexities of deadly neurodegenerative disease; offers promising strategies to target disease’s underlying genetic mechanisms
New ‘more effective’ stem cell transplant method could aid blood cancer patients
Peer reviewed | experimental study | animals
New therapeutic strategy against diabetes
Maintaining vitamin D receptor levels in insulin-producing cells could protect against diabetes
Edmonton company Entos developing DNA vaccine against COVID-19
University of Alberta cancer researcher John Lewis’s health-care biotechnology company is working on a vaccine to be delivered directly into patients’ cells, driving a protective immune response.
Tracking adeno-associated virus capsid evolution
New Rochelle, NY, March 18, 2020–Researchers have used high-throughput screening of adeno-associated viral (AAV) vector capsid libraries to maximize the likelihood of obtaining AAV variants with desired properties. As a result of these experiments, they gained some unexpected insights, reported…