The vision of people with a rare inherited condition that causes them to lose much of their sight early in childhood was 100 times better after they received gene therapy to address the genetic mutation causing it. Some patients even experienced a 10,000-fold improvement in their vision after receiving the highest dose of the therapy, according to researchers from the Perelman School of Medicine at the University of Pennsylvania who co-led the clinical trial published in The Lancet.
Tag: ophthalmalogy
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$2.6 million in grant funding to support research on genetic causes of blindness
Indiana University School of Medicine’s Yoshikazu Imanishi, PhD, was recently awarded a four-year, $2.1 million grant from the National Eye Institute and a three-year, $500,000 grant from the Foundation Fighting Blindness to study genetic causes of blindness.