Elevidys Gene Therapy: A Neurologist’s Perspective

Over the past year, Children’s Hospital Los Angeles has been one of the highest-volume centers in the nation for Elevidys gene therapy. So far, CHLA has treated 10 boys with Duchenne muscular dystrophy with this gene transfer therapy—among the most in the U.S.Leading these efforts at CHLA is Leigh Ramos-Platt, MD, Director of the Neuromuscular Disorders Center in the Neurological Institute at Children’s Hospital Los Angeles, which includes one of the largest programs in California for Duchenne.