Scientists publish encouraging early tests of a gene therapy strategy against Angelman syndrome, a neurodevelopmental disorder that features poor muscle control and balance, hard-to-treat epilepsy, and intellectual disabilities.
Tag: Angelman Syndrome
FAST Conference Draws 20 Pharmaceutical Companies and Raises Over $2.2 Million for Research on Angleman Syndrome
FAST (the Foundation for Angelman Syndrome Therapeutics) today announced that Virtually Unstoppable, their annual Summit & Gala benefitting Angelman syndrome (AS) raised over $2.2 million during their virtual two-day conference.