Researchers hope at least one will treat progressive blindness caused by Usher syndrome type 1F
Tag: Usher Syndrome
Toward a Therapy for a Rare Genetic Disease
Researchers design “mini gene” therapy for severe syndrome that causes blindness and deafness
NIH Funds Miller School Researcher’s Novel Work to Develop Gene Therapy for Hearing Loss-related Usher Syndrome
The National Institute on Deafness and Other Communication Disorders (NIDCD) has awarded Xue Zhong Liu, M.D., Ph.D., Marian and Walter Hotchkiss Endowed Chair in Otolaryngology at the University of Miami Miller School of Medicine, a five-year, $3.5 million R01 research grant to develop a precision medicine approach to treat hearing loss (HL) in Usher syndrome (USH).