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Tag: Gene Therapy
Researchers create functional mini-liver by 3D bioprinting
Technique developed at Human Genome and Stem Cell Research Center, funded by FAPESP and hosted by the University of São Paulo, produced hepatic tissue in the laboratory in only 90 days and could become an alternative to organ transplantation in future
Researchers create functional mini-liver by 3D bioprinting
Technique developed at Human Genome and Stem Cell Research Center, funded by FAPESP and hosted by the University of São Paulo, produced hepatic tissue in the laboratory in only 90 days and could become an alternative to organ transplantation in future
A new gene therapy strategy, courtesy of Mother Nature
Scientists have developed a new gene-therapy technique by transforming human cells into mass producers of tiny nano-sized particles full of genetic material that has the potential to reverse disease processes.
A new gene therapy strategy, courtesy of Mother Nature
Scientists turn a natural cellular process into a drug-delivery system
A new gene therapy strategy, courtesy of Mother Nature
Scientists turn a natural cellular process into a drug-delivery system
IU School of Medicine team learns how to predict triple negative breast cancer recurrence
Discovery marks progress in IU Precision Health Initiative Grand Challenge
IU School of Medicine team learns how to predict triple negative breast cancer recurrence
Discovery marks progress in IU Precision Health Initiative Grand Challenge
Increasing food intake by swapping mitochondrial genomes
Many of the characteristics that make people so different from each other, are often the result of small differences in the DNA between individuals. Variation in just a single base in our DNA can cause significant variation in traits like…
Increasing food intake by swapping mitochondrial genomes
Many of the characteristics that make people so different from each other, are often the result of small differences in the DNA between individuals. Variation in just a single base in our DNA can cause significant variation in traits like…
Janus bases among The Scientist’s Top Innovations of 2019
Invented at Carnegie Mellon, the bivalent nucleic acid recognition platform is being used to develop treatments for rare genetic diseases
Janus bases among The Scientist’s Top Innovations of 2019
Invented at Carnegie Mellon, the bivalent nucleic acid recognition platform is being used to develop treatments for rare genetic diseases
GW-led consortium receives $2.2 million grant to fund BioCompute Object Specification Project
The BioCompute Object Specification Project works to standardize genomic data analysis
GW-led consortium receives $2.2 million grant to fund BioCompute Object Specification Project
The BioCompute Object Specification Project works to standardize genomic data analysis
Wellcome Trust establishes first translational partnership in Germany with Charité and the BIH
Charité – Universitätsmedizin Berlin and the Berlin Institute of Health (BIH) are the first institutions in Germany to receive funding to create a translational partnership with the UK-based Wellcome Trust. Via its translational partnerships, the Wellcome Trust supports institutions in…
Wellcome Trust establishes first translational partnership in Germany with Charité and the BIH
Charité – Universitätsmedizin Berlin and the Berlin Institute of Health (BIH) are the first institutions in Germany to receive funding to create a translational partnership with the UK-based Wellcome Trust. Via its translational partnerships, the Wellcome Trust supports institutions in…
A lifeline for leaky lung cells
AAV-based gene therapy reduces vascular leakage in human Lung Chip, could lead to pulmonary edema treatment
A lifeline for leaky lung cells
AAV-based gene therapy reduces vascular leakage in human Lung Chip, could lead to pulmonary edema treatment
Using gene scissors to detect diseases
The CRISPR/Cas technology can do more than alter genes. A research team at the University of Freiburg is using what are known as gene scissors – which scientists can use to edit genetic material – in order to better diagnose…
Using gene scissors to detect diseases
The CRISPR/Cas technology can do more than alter genes. A research team at the University of Freiburg is using what are known as gene scissors – which scientists can use to edit genetic material – in order to better diagnose…
Fred Hutch at ASH: Latest CAR T data – BCMA, CD19, CD20 – plus new insights on transplantation, gene therapy – and more
The 61st American Society of Hematology Annual Meeting and Exposition will take place Dec. 7–10 in Orlando, Florida
Simulations suggest embryo selection based on traits like height or IQ is still far off
There have been concerns about the idea of “designer babies” for almost as long as in vitro fertilization and technology to screen embryos for inherited disorders have existed. While the recent live births resulting from human embryonic CRISPR editing have…
Simulations suggest embryo selection based on traits like height or IQ is still far off
There have been concerns about the idea of “designer babies” for almost as long as in vitro fertilization and technology to screen embryos for inherited disorders have existed. While the recent live births resulting from human embryonic CRISPR editing have…
‘Combo’ nanoplatforms for chemotherapy
In a paper to be published in the forthcoming issue in NANO , researchers from Harbin Institute of Technology, China have systematically discussed the recent progresses, current challenges and future perspectives of smart graphene-based nanoplatforms for synergistic tumor therapy and…
Gene therapy: Development of new DNA transporters
Scientists at the Institute of Pharmacy at Martin Luther University Halle-Wittenberg (MLU) have developed new delivery vehicles for future gene therapies. A team of researchers led by Dr Christian Wölk are using artificial fats to transport DNA into cells. The…
Gene therapy: Development of new DNA transporters
Scientists at the Institute of Pharmacy at Martin Luther University Halle-Wittenberg (MLU) have developed new delivery vehicles for future gene therapies. A team of researchers led by Dr Christian Wölk are using artificial fats to transport DNA into cells. The…
Precisely poking cells en masse to cure cancer
Device can mass-produce engineered cells at lower cost, a tipping point for emerging lifesaving therapies
Precisely poking cells en masse to cure cancer
Device can mass-produce engineered cells at lower cost, a tipping point for emerging lifesaving therapies
Delivering large genes to the retina is problematic
New Rochelle, NY, November 12, 2019–A new study has shown that a commonly used vector for large gene transfer can successfully deliver genes to retinal cells in the laboratory, but when injected subretinally into rats it provokes a robust and…
Delivering large genes to the retina is problematic
New Rochelle, NY, November 12, 2019–A new study has shown that a commonly used vector for large gene transfer can successfully deliver genes to retinal cells in the laboratory, but when injected subretinally into rats it provokes a robust and…
Modified CRISPR gene editing tool could improve therapies for HIV, sickle cell disease
City of Hope’s cell experiments show more effective genetic ‘cuts’ that could one day become the foundation of new and more effective gene therapies
New molecule reduces the aggressiveness of pediatric cancer
A microRNA inhibitor identified by researchers at the FAPESP-supported Human Genome and Stem Cell Research Center reduced the sizes of aggressive tumors and improved survival in mice
A mechanism capable of preserving muscle mass
A promising avenue for the prevention of sarcopenia
A new CRISPR-Cas9 protein to increase precision of gene editing
A team of researchers from City University of Hong Kong (CityU) and Karolinska Institutet has recently developed a new protein that can help increase the targeting accuracy in the genome editing process. It is believed that it would be useful…
A mechanism capable of preserving muscle mass
A promising avenue for the prevention of sarcopenia
A new CRISPR-Cas9 protein to increase precision of gene editing
A team of researchers from City University of Hong Kong (CityU) and Karolinska Institutet has recently developed a new protein that can help increase the targeting accuracy in the genome editing process. It is believed that it would be useful…
Unique case of disease resistance reveals possible Alzheimer’s treatment
NIH-funded study identifies gene variant as potential drug target
Unique case of disease resistance reveals possible Alzheimer’s treatment
NIH-funded study identifies gene variant as potential drug target
EMBL spins the Sleeping Beauty transposase
New possibilities for gene therapies
Combination gene therapy treats multiple age-related diseases
Treatment increases healthspan in mice and could lead to increased longevity
Combination gene therapy treats multiple age-related diseases
Treatment increases healthspan in mice and could lead to increased longevity
Unique case of disease resistance reveals possible Alzheimer’s treatment
NIH-funded study identifies gene variant as potential drug target
Combination gene therapy treats multiple age-related diseases
Treatment increases healthspan in mice and could lead to increased longevity
EMBL spins the Sleeping Beauty transposase
New possibilities for gene therapies
EMBL spins the Sleeping Beauty transposase
New possibilities for gene therapies
New nonprofit organization formed to accelerate drug development in autism-associated genetic conditions
LOS ANGELES, CA, October 23, 2019 – Parents of children affected by Phelan-McDermid syndrome (PMS) announce the formation of CureSHANK, a nonprofit organization to accelerate drug development in PMS and other diseases related to the SHANK genes. As one of…
By cutting out one gene, researchers remove a tadpole’s ability to regenerate
Tadpoles of frogs that can typically regrow amputated tails or limbs lost their ability to regenerate after researchers blocked the expression of a newly identified gene that is one of the drivers for this regrowth. Furthermore, scientists hypothesize that the…
Beverly Davidson, PhD, Elected to the National Academy of Medicine
Beverly L. Davidson, PhD, director of the Raymond G. Perelman Center for Cellular and Molecular Therapeutics at Children’s Hospital of Philadelphia, has been elected to the National Academy of Medicine. She is being recognized for her role in developing innovative therapies for fatal, inherited brain disorders.
Stephan Grupp, MD, PhD, elected to National Academy of Medicine
Children’s Hospital of Philadelphia physician-scientist receives outstanding honor in medicine for work in cell and gene therapy
Realizing the potential of gene therapy for neurological disorders
Advances in gene therapy may aid future treatments of Alzheimer’s disease, Parkinson’s disease, and more